Sickle Cell

Just published in the New England Journal of Medicine. A new gene-splicing technology called CRISPR seems to be working. 44 patients received this new technology. All of the patients had sickle cell. All patients had been admitted to the hospital at least twice yearly for the previous two years with sickle crisis. Of the 30 patients who had adequate follow-up, 29 didn’t have any hospitalizations for sickle crisis in the subsequent 12 months. This is really GREAT news.

It must be remembered that this is a preliminary study. These early studies almost always look good. We need to wait for further studies. These patients didn’t seem to have any significant side effects.

You can find the original article here.

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